Developing a Newborn Screening Toolkit for Adrenoleukodystrophy: Key Learnings

Time: 1:30 pm
day: Day One


  • Understanding the importance of newborn screening in the context of gene therapy
  • Collaborating with patient communities on development of an advocacy toolkit specifically focused on newborn screening
  • Exploring what went well, but also what improvements could be made to the process for future projects given what is known now