Setting the Scene: Progress of Gene Therapy so Far in the Context of Patient Centricity

Time: 8:30 am
day: Day One


  • Patients are central to any drug development process – what makes gene therapy unique in terms of incorporating the patient voice effectively?
  • Understanding the increased industry presence particularly within rare disease, and how this has altered stakeholder perspectives and priorities
  • Achieving success (or failure) of gene therapy programs is impacted by how effectively patient values are both heard and actioned