Speakers

Alison Bateman-House

Assistant Professor, Department of Population Health

NYU

Amy Fisher

Head of Patient Advocacy

Spark Therapeutics

Anne Rowzee

Associate Director for Policy, CBER

FDA

Annie Ganot

Founder & VP Patient Advocacy

Solid Biosciences

Craig Martin

CEO

Global Genes

Edgar Vega

Senior Manager, Patient Advocacy

uniQure

Halley Losekamp

Director, Patient Enrolment

AGTC

Jennifer Helfer

Head, Patient Advocacy & Engagement

Encoded Therapeutics

Jodi Wolff

VP, Patient Engagement & Advocacy

StrideBio

Jordanna Mora

Senior Director, Patient Advocacy & Centricity

Beam Therapeutics

Karen Jackler

Program Manager, Patient Engagement, CBER

FDA

Kate Trenam

Head of Patient Engagement, Early Research

UCB

Kristen Huehbner

Associate Director, Global Patient Advocacy & Engagement

BioMarin

Kristin Voorhees

Director, Patient Advocacy

Ultragenyx

Pat Furlong

Founding President & CEO Parent Project Muscular Dystrophy

Parent Project Muscular Dystrophy

Paula Orandash

Patient Engagement Liaison, Community Education Gene Therapy

PTC Therapeutics

PJ Brooks

Deputy Director, Officer of Rare Diseases Research

NIH

Safiyya Gassman

Senior Director, Policy & Public Affairs

Pfizer

Sara Davis

Senior Director, Patient Advocacy & Government Affairs

CRISPR Therapeutics

Sarah Friedhoff

Associate Director, Patient Advocacy & Clinical Affairs

Abeona Therapeutics

Tom Croce

VP, Patient Advocacy

bluebird bio

Vivian Fernandez

Senior Director, Patient Advocacy

REGENXBIO

Wendy Borsari

Senior Manager, Patient Advocacy

Tenaya Therapeutics

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