Speakers Alison Bateman-House Assistant Professor, Department of Population Health NYU Amy Fisher Head of Patient Advocacy Spark Therapeutics Anne Rowzee Associate Director for Policy, CBER FDA Annie Ganot Founder & VP Patient Advocacy Solid Biosciences Craig Martin CEO Global Genes Edgar Vega Senior Manager, Patient Advocacy uniQure Halley Losekamp Director, Patient Enrolment AGTC Jennifer Helfer Head, Patient Advocacy & Engagement Encoded Therapeutics Jodi Wolff VP, Patient Engagement & Advocacy StrideBio Jordanna Mora Senior Director, Patient Advocacy & Centricity Beam Therapeutics Karen Jackler Program Manager, Patient Engagement, CBER FDA Kate Trenam Head of Patient Engagement, Early Research UCB Kristen Huehbner Associate Director, Global Patient Advocacy & Engagement BioMarin Kristin Voorhees Director, Patient Advocacy Ultragenyx Pat Furlong Founding President & CEO Parent Project Muscular Dystrophy Parent Project Muscular Dystrophy Paula Orandash Patient Engagement Liaison, Community Education Gene Therapy PTC Therapeutics PJ Brooks Deputy Director, Officer of Rare Diseases Research NIH Safiyya Gassman Senior Director, Policy & Public Affairs Pfizer Sara Davis Senior Director, Patient Advocacy & Government Affairs CRISPR Therapeutics Sarah Friedhoff Associate Director, Patient Advocacy & Clinical Affairs Abeona Therapeutics Tom Croce VP, Patient Advocacy bluebird bio Vivian Fernandez Senior Director, Patient Advocacy REGENXBIO Wendy Borsari Senior Manager, Patient Advocacy Tenaya Therapeutics FULL EVENT GUIDE WORKSHOP DAY