Speakers

Alison Kujawski

Senior Outreach Manager

American Society of Cell & Gene Therapy

Andrea Wilkinson

Global Head Patient Engagement

UCB

Behtash Bahador

Director, Health Literacy

CISCRP

Bethany Firem

Associate Director, Global Patient Affairs

BioMarin Pharmaceutical Inc.

Betsy Bogard

Board Member

Global Genes

Brendan Hayes

Director of Education, Innovative Therapies

National Hemophilia Foundation

Brian O’Mahony

Chief Executive Officer

Irish Haemophilia Society

Craig Martin

President

Rithm Health

Daniel Leonard

Senior Director - Global Patient Advocacy

uniQure

David Rintell

Head of Patient Advocacy

BridgeBio

Jean-Pierre Malkowski

ED Patient Engagement Center of Excellence

Novartis AG

Jennifer Helfer

Senior Director, Patient Advocacy & Engagement, Corporate Affairs

Viridian Therapeutics

Jennifer McNary

Co-founder and Principal

Canary Advisors LLC

Jessica Riviere

Vice President, Global Patient Advocacy & Patient Engagement

Ultragenyx

Mandy Rohrig

Associate Director, Patient Advocacy BridgeBio Gene Therapy

BridgeBio

Melissa Penn

Director - Patient Engagement Research & Development

Bayer

Mindy Cameron

President

AdvocacyWorks

Nan Doyle

Associate Director, Patient Insights - Rare Diseases Drug Discovery Unit

Takeda

Sara Johnson Davis

Senior Director, Patient Advocacy & Government Affairs

CRISPR Therapeutics

Sujan Sivasubramaniyam

Head of Medical Affairs

CSL Behring

Susan Brisendine

Director, Patient Advocacy

bluebird bio

Thomas Bols

Head of Government Affairs and Patient Advocacy, EMEA

PTC Therapeutics