EXPERT SPEAKERS Amanda Rohrig Director, Patient Advocacy Bridge Bioscience Corp Behtash Bahador Director - Health Literacy CISCRP Christine Slater Associate Director, Patient Recruitment Editas Medicine Craig Kessler Professor Georgetown University Felice Tsui Associate Director of Patient Advocacy Editas Medicine Jennifer Helfer Patient Advocacy & Engagement Viridian Therapeutics Jewell Martin Director, US Regulatory Policy BioMarin Pharmaceutical Kara Fick Director - Patient Advocacy & Medical Affairs Atsena Therapeutics Karen Utley President and Co-Founder International Foundation for CDKL5 Research Kristin Voorhees Director, Patient Advocacy Ultragenyx LEONARD VALENTINO PROFESSOR, ENTREPRENEUR IN RESIDENCE, PATHWAY TO CURES Rush University Lesley Milliner Senior Patient Education Liaison Spark Therapeutics Matt Giordano Senior Director of Patient Access and Advocacy Krystal Biotech Michaela Jones Global Medical Affairs, Hemophilia Gene Therapy (CRISPR/Cas9) & Thrombosis Regeneron Pharmaceuticals Inc Nan Doyle Principal Takeda Pharmaceutical Co. Ltd. Natacha Raphael Regional Head, Corporate Affairs and Patient Advocacy Biogen Oscar Segurado Chief Medical Officer ASC Therapeutics Pam Rattananont Director, Patient Advocacy Novartis Paul Sommer Global Head Of Patient Experience & Innovation Decibel Therapeutics Inc. Su Smith Head of Patient Strategy Origins Susan Brisendine Director, Patient Advocacy bluebird bio Tara Hastings Patient Engagement Lead, Rare Diseases Sanofi Tiara Johnson Associate Director, Global Patient Affairs BioMarin Pharmaceutical Wendy Borsari Associate Director Patient Advocacy Tenaya Therapeutics EVENT GUIDE ABOUT REGISTER